Hemophilia Research Paper

Improved Essays
Hemophilia is a genetic disease that causes an affected person to severely bleed if cut. Lucky for hemophilia patients, gene therapy is an option. Gene therapy is a form of therapy during which selected healthy genes are transferred to an affected person’s cells. Not only is gene therapy a breakthrough in genetic engineering, but it can effectively cure genetic disorders such as cystic fibrosis and SCID and some acquired diseases like cancer. Gene therapy is carried out by packing a section of DNA into a vector, such as a virus or a plasmid, which is carried into the patient’s affected cell. Soon after, the new DNA is expressed and the correct proteins are produced, treating the genetic disease. There are two types of gene therapy: somatic

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