Genetic Engineering : Gene Therapy Essay

1586 Words Dec 14th, 2016 7 Pages
Gene therapy is a technique in genetic engineering that is used to introduce new genetic material into host cells. This technique has become an invaluable tool in correcting faulty genes in order to improve the overall health of patients affected by both genetic disorders and non-genetic diseases. It has been documented that most human diseases occur as a result of a mutation in a single gene or a set of genes that code for important proteins needed for survival (1). Some of the genetic and non-genetic disorders that gene therapy is being used to study and treat are Parkinson’s disease, Amyotrophic Lateral Sclerosis (ALS), Epilepsy, and Alzheimer’s disease, cancer, Cystic Fibrosis as well as glial cell reconstruction (.
Although there are different methods of gene therapy, this therapy starts with the identification of the faulty or mutant gene that is responsible for the diseased state. The next step is cloning a healthy version of the identical gene which is usually called a therapeutic gene as it should elicit a therapeutic effect. The therapeutic gene is genetically altered with specific instruction to perform a particular purpose. After this, the therapeutic gene is loaded in a transporter known as a vector. The function of the vector is to deliver the therapeutic gene to the faulty target cells. After the vector reaches the intended cells, it delivers the therapeutic gene to the nucleus and the new genetic material is integrated into the DNA of the cell in order to…

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