Cystic Fibrosis: Gene Therapy Research

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Gene therapy is where normal genes/ genetic material are inserted into the cell where missing or malfunctioning genes are, potentially correcting any disorders caused by the faulty gene. Leading research of gene therapy to treat Cystic Fibrosis has made ground breaking discoveries in ways in which faulty or missing CFTR genes (responsible for moving salt and water out of cells) can be replaced via Vectors, to ensure the protein can regain its normal function. This annotated bibliography provides specifics of key findings and effects gene therapy has in regards to treating Cystic Fibrosis.
1. Burney, Davies, Jane C, Tabinda J 2007, NCBI, The application of clinical genetics, Vol.5, pp.29-36 This paper has described to the reader the reason

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